Defined term · Outcomes and endpoints
Efficacy
The effect of an intervention under the conditions of a controlled trial, in a selected population with protocol-driven adherence and follow-up.
§1Efficacy
§1.2Category
Outcomes and endpoints — Terms describing what a study measures and what the measurement supports.
§1.3Related terms
- Effectiveness — The effect of an intervention under ordinary conditions of use. Generally smaller than efficacy, principally because adherence and persistence outside a trial are lower.
Compound Evidence Institute · CEI-GT-031 · https://compoundevidence.com/glossary/efficacy/ · retrieved 30 July 2026